Højdepunkter fra ASGCT 23. årsmøde
AAV-integrationsanalyse efter langvarig opfølgning i hæmofili A Hunde afslører de genetiske konsekvenser af AAV-medieret genkorrektion
John K. Everett1, Giang N. Nguyen2, Hayley Raymond1, Aiofe Roche1, Samita Kafle2, Christian Wood2, Jacob Leiby1, Elizabeth P. Merricks3, Haig H. Kazazian4, Timothy C. Nichols3, Frederic D. Bushman1, Denise E. Sabatino2,5
1Institut for Mikrobiologi, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
2Raymond G. Perelman Center for Cellular and Molecular Therapeutics, Børnehospitalet i Philadelphia, Philadelphia, PA
3Institut for Patologi og Laboratoriemedicin, University of North Carolina, Chapel Hill, NC
4Institut for genetisk medicin, Johns Hopkins School of Medicine, Baltimore, MD
5Institut for Pædiatri, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
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