Highlights From the 62nd ASH Annual Meeting and Exposition
AMT-060 Gene Therapy in Adults With Severe or Moderate-Severe Hemophilia B Confirm Stable FIX Expression and Durable Reductions in Bleeding and Factor IX Consumption for Up to 5 Years
Frank W.G. Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michiel Coppens, MD3, Peter Kampmann, MD4, Robert Klamroth, MD, PhD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble9, Halvard Bönig1,10, Eileen K K Sawyer, PhD11, and Wolfgang A. Miesbach, MD12
1Erasmus University Medical Center, Rotterdam, Netherlands
2Dept. of Hematology, University of Groningen, University Medical Center Groningen, Groningen, Netherlands
3Amsterdam University Medical Center, University of Amsterdam, Amsterdam, Netherlands
4Rigshospitalet, Copenhagen, Denmark
5Department for Internal Medicine, Vascular Medicine and Haemostaseology, Vivantes Klinikum im Friedrichshain, Berlin, Germany
6Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Universitaria Careggi, Florence, Italy
8Institute Frankfurt, German Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
9Institute Frankfurt, German Red Cross Blood Service Baden-Wurttemberg-Hessen, Frankfurt, Germany
10University of Washington School of Medicine, Seattle, WA
11uniQure Inc., Lexington, MA
12Universitatsklinikum Frankfurt, Frankfurt, Germany
Frank W.G. Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michiel Coppens, MD3, Peter Kampmann, MD4, Robert Klamroth, MD, PhD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble9, Halvard Bönig1,10, Eileen K K Sawyer, PhD11, and Wolfgang A. Miesbach, MD12
1Erasmus University Medical Center, Rotterdam, Netherlands
2Dept. of Hematology, University of Groningen, University Medical Center Groningen, Groningen, Netherlands
3Amsterdam University Medical Center, University of Amsterdam, Amsterdam, Netherlands
4Rigshospitalet, Copenhagen, Denmark
5Department for Internal Medicine, Vascular Medicine and Haemostaseology, Vivantes Klinikum im Friedrichshain, Berlin, Germany
6Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Universitaria Careggi, Florence, Italy
8Institute Frankfurt, German Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
9Institute Frankfurt, German Red Cross Blood Service Baden-Wurttemberg-Hessen, Frankfurt, Germany
10University of Washington School of Medicine, Seattle, WA
11uniQure Inc., Lexington, MA
12Universitatsklinikum Frankfurt, Frankfurt, Germany