Highlights From the ISTH 2021 Congress
Clinical Outcomes in Adults With Hemophilia B With and Without Pre-existing Neutralizing Antibodies to AAV5: 6 Month Data From the Phase 3 Etranacogene Dezaparvovec HOPE-B Gene Therapy Trial
F.W. Leebeek1, W. Miesbach2, M. Recht3, N.S Key4, S. Lattimore3, G. Castaman5, E.K Sawyer6,7, D. Cooper6,7, V. Ferriera6,7, S.W Pipe8, HOPE-B Investigators
1Erasmus University Medical Center, Rotterdam, Netherlands
2University Hospital Frankfurt, Frankfurt, Germany
3Oregon Health & Science University, Portland, United States
University of North Carolina, Chapel Hill, United States
5Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
6uniQure BV, Amsterdam, Netherlands
7uniQure Inc, Lexington, United States
8University of Michigan, Ann Arbor, United States
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