Aspectes destacats del 14è Congrés Anual d'EAHAD
Seguiment d'una nova teràpia gènica amb virus associat a l'adeno (AAV) (FLT180a) per assolir nivells normals d'activitat FIX en pacients amb hemofília severa B (HB)
(Estudi B-AMAZE)
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kate parla,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, Londres, Regne Unit
2University College London, Londres, Regne Unit
3Oxford Haemophilia Center, Oxford, Regne Unit
4Universitat de Sheffield, Sheffield, Regne Unit
5Kent i Canterbury Hospital, Canterbury, Regne Unit
6Hospital Universitari de Southampton, Southampton, Regne Unit
7Newcastle Haemophilia Comprehensive Care Center, Newcastle, Regne Unit
8St Thomas 'and Guy's Hospital, Londres, Regne Unit
9St Jude Children's Research, Memphis, TN, EUA
10Freeline, Stevenage, Regne Unit
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kate parla,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, Londres, Regne Unit
2University College London, Londres, Regne Unit
3Oxford Haemophilia Center, Oxford, Regne Unit
4Universitat de Sheffield, Sheffield, Regne Unit
5Kent i Canterbury Hospital, Canterbury, Regne Unit
6Hospital Universitari de Southampton, Southampton, Regne Unit
7Newcastle Haemophilia Comprehensive Care Center, Newcastle, Regne Unit
8St Thomas 'and Guy's Hospital, Londres, Regne Unit
9St Jude Children's Research, Memphis, TN, EUA
10Freeline, Stevenage, Regne Unit