Highlights From the 14th Annual Congress of EAHAD
AMT-060 Gene Therapy in Adults With Severe or Moderate-Severe Hemophilia B Confirm Stable FIX Expression and Durable Reductions in Bleeding and Factor IX Consumption for Up to 5 Years
Frank W.G. Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michiel Coppens, MD, PhD3, Peter Kampmann, MD4, Robert Klamroth, MD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble, MD9, Halvard Bönig, MD1,10, Eileen K. Sawyer, PhD11, and Wolfgang Miesbach, MD, PhD12
1Erasmus University Medical Center, Rotterdam, Netherlands
2University Medical Center Groningen, Groningen, Netherlands
3Amsterdam University Medical Center, Amsterdam, Netherlands
4Rigshospitalet, Copenhagen, Denmark
5Vivantes Klinikum, Berlin, Germany
6Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Universitaria Careggi, Florence, Italy
8Institute Frankfurt, German Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
9Institute Frankfurt, German Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
10University of Washington, Seattle, WA
11uniQure Inc., Lexington, MA
12University Hospital Frankfurt, Frankfurt, Germany
Frank W.G. Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michiel Coppens, MD, PhD3, Peter Kampmann, MD4, Robert Klamroth, MD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble, MD9, Halvard Bönig, MD1,10, Eileen K. Sawyer, PhD11, and Wolfgang Miesbach, MD, PhD12
1Erasmus University Medical Center, Rotterdam, Netherlands
2University Medical Center Groningen, Groningen, Netherlands
3Amsterdam University Medical Center, Amsterdam, Netherlands
4Rigshospitalet, Copenhagen, Denmark
5Vivantes Klinikum, Berlin, Germany
6Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Universitaria Careggi, Florence, Italy
8Institute Frankfurt, German Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
9Institute Frankfurt, German Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
10University of Washington, Seattle, WA
11uniQure Inc., Lexington, MA
12University Hospital Frankfurt, Frankfurt, Germany