ISTH Gene Therapy Steering Committee

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Flora Peyvandi, MD, PhD (Co-Chair)

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David Lillicrap, MD
(Co-Chair)

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Pratima Chowdary, MD, MRCP, FRCPATH

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Johnny Mahlangu, BSc, MBBCh, MMed, FCPath

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Wolfgang A. Miesbach, MD, PhD

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Margareth C. Ozelo, MD, PhD

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Glenn F. Pierce, MD, PhD

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Steven W. Pipe, MD

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Alok Srivastava, MD, FRACP, FRCPA, FRCP

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Thierry VandenDriessche, PhD

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Supported through educational grants from BioMarin, CSL Behring, Pfizer Inc., Roche, and Spark Therapeutics

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