Latest News

 

Science Translational Medicine (05/22/19) Vol. 11, No. 493 Milani, Michela; Annoni, Andrea; Moalli, Federica; et al.

 

Haemophilia (05/21/19) Miesbach, W.; O'Mahoney, B.; Key, N.S.; et al.

 

Research and Practice in Thrombosis and Haemostasis (Spring 2019) Vol. 3, No. 2, P. 261 Stanford, S.; Pink, R.; Creagh, D.; et al.

 

Research and Practice in Thrombosis and Haemostasis (Spring 2019) Vol. 379, No. 20, P. 184 Konkle, Barbara A.; Skinner, Mark; Iorio, Alfonso

 

Science Translational Medicine (05/22/19) Vol. 11, No. 493 Milani, Michela; Annoni, Andrea; Moalli, Federica; et al.

Conference Coverage – Live from ISTH 2019 in Melbourne

The ALTA Study: SB-525 Gene Therapy in Adults with Hemophilia A
Prevalence of Preexisting AAV Antibodies and Implications for Gene Therapy in Hemophilia
Results of the AMT-060 and AMT-061 Gene Therapy Trials in Patients with Hemophilia B
Initial Results of the Phase 1/2 Alta Study: SB-525 Gene Therapy in Adults with Hemophilia A
One Year Follow-up of Patients with Hemophilia B Following SPK-9001 Gene Transfer
AMT-061 Gene Transfer in Adults with Hemophilia B: Early Results of a Phase 2b Trial
Current Status of Gene Therapy for Hemophilia
FLT180a: Next Generation AAV Vector for Hemophilia B
Stable Expression of FIX: Updated Results of the AMT-060 Gene Therapy Trial in Patients with Hemophilia B.
Lentiviral Vector-based Factor VIII and Factor IX Gene Therapy in Non-human Primates
Valoctocogene Roxaparvovec AAV Gene Therapy for Patients with Hemophilia A: New Results
Looking Ahead at Gene Therapy for Hemophilia